According to the Mayo Clinic, Rett syndrome is a developmental disorder that affects the way the brain develops Courtesy of Shelly Balboa When Joseph and Shelly Balboa's daughter was 2 months old, the ...

TULSA, Okla. — At almost 3 years old, Elaina Donahue is a happy child who likes to play with water and socks, but Elaina has spent most of her life in and out of the hospital. At just a year old, ...

Taysha Gene Therapies has unfurled more data in the developmental disorder Rett syndrome, linking its gene therapy to improvements in the first adults and children to receive low doses of the ...

Texas Children's Hospital, an internationally-recognized, top-ranked children's hospital and pediatric research center affiliated with Baylor College of Medicine, is the first to deliver a novel gene ...

Researchers at Baylor College of Medicine, Jan and Dan Duncan Neurological Research Institute (Duncan NRI) at Texas Children’s Hospital and collaborating institutions have gained new insights into the ...

Scientists investigating the severe developmental disorder known as Rett syndrome have discovered a series of crucial molecular changes that occur long before symptoms appear. The findings could be ...

Texas Children’s Hospital, an internationally-recognized, top-ranked children’s hospital and pediatric research center affiliated with Baylor College of Medicine, is the first to deliver a novel gene ...

Anavex released data from the EXCELLENCE trial, designed to evaluate ANAVEX 2-73 in 92 children aged 5-17 with Rett syndrome. The trial had two co-primary endpoints, Rett Syndrome Behaviour ...

On an unseasonably warm day in late February, scientists at Kunming Medical University’s Experimental Animal Center in the far southwestern province of Yunnan injected a female crab-eating macaque ...

Feb. 11 -- TUESDAY, Feb. 10 (HealthDay News) -- Researchers may have found a new treatment for Rett syndrome, a rare inherited disease in girls that brings on autism-like symptoms along with heart and ...

NEW YORK--(BUSINESS WIRE)--Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, ...