The Phase 1/2 trial is a first-in-human, open-label, multi-national study designed to evaluate the safety, tolerability, and efficacy of TSRA-196 in adults with AATD. Trial participants will receive a ...

Thanks to genetic science, gene editing, and techniques like cloning, it’s now possible to move DNA through time, studying ...

The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...

A new CRISPR approach can control genes without cutting DNA, opening a safer path for treating genetic diseases. A newly ...

An international team including researchers from Nvidia and Microsoft has used AI on a biological trove of more than a ...

Complexities like these make it challenging to develop broadly applicable gene therapies for these disorders. Researchers at The University of Texas at Austin now have developed an improved method of ...

Joint Statement by Ralph J. Cicerone and Victor J. Dzau WASHINGTON -- The National Academy of Sciences and the National Academy of Medicine are launching a major initiative to guide decision making ...

A multidisciplinary committee of experts studied the scientific underpinnings of human gene-editing technologies, their potential use in biomedical research and medicine -- including human germline ...

Almost 100 years ago, Carrie Buck was raped, labeled an “imbecile,” and sterilized by order of the state — all in the name of genetic progress. Today, we no longer use that word, but the dream of ...

Like other developing countries, Indonesia is facing a familiar dilemma: how to feed a growing population while protecting ...