The Phase 1/2 trial is a first-in-human, open-label, multi-national study designed to evaluate the safety, tolerability, and efficacy of TSRA-196 in adults with AATD. Trial participants will receive a ...

An international team including researchers from Nvidia and Microsoft has used AI on a biological trove of more than a ...

The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...

Thanks to genetic science, gene editing, and techniques like cloning, it’s now possible to move DNA through time, studying ...

A new CRISPR approach can control genes without cutting DNA, opening a safer path for treating genetic diseases. A newly ...

Complexities like these make it challenging to develop broadly applicable gene therapies for these disorders. Researchers at The University of Texas at Austin now have developed an improved method of ...

That rogue scientist who created HIV-resistant designer babies is apparently gearing up for more human gene-editing research. In an interview with the Wall Street Journal, He Jiankui said he wants to ...

Data Demonstrate Potent in vivo Gene Editing of Hematopoietic Stem Cells (HSCs) in the Bone Marrow with Systemic Delivery in Preclinical Murine Models Using Fusogen Technology Broadens Application of ...

Joint Statement by Ralph J. Cicerone and Victor J. Dzau WASHINGTON -- The National Academy of Sciences and the National Academy of Medicine are launching a major initiative to guide decision making ...

Like other developing countries, Indonesia is facing a familiar dilemma: how to feed a growing population while protecting ...