Explore how researchers are using next-generation CRISPR therapies to target the root cause of muscle degeneration.

Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. Researchers show how a dual CRISPR RNA method restored dystrophin protein ...

Researchers from Kyoto University demonstrate how a dual CRISPR RNA method restored dystrophin protein function in induced pluripotent stem cells derived from Duchenne muscular dystrophy (DMD) ...

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. Two of the first efforts to treat Duchenne ...

ALAMEDA, Calif.--(BUSINESS WIRE)-- Scribe Therapeutics Inc. (Scribe), a genetic medicines company unlocking the potential of CRISPR to transform human health, today announced its participation in the ...

Left: Muscle fibers expressing dysferlin (purple) made from gene-edited muscle stem cells transplanted into a mouse that lacks dysferlin. Right: Muscle fibers from the recipient mouse that are ...

TOKYO & WALTHAM, Mass.--(BUSINESS WIRE)--Modalis Therapeutics Corporation (Tokyo Stock Exchange: 4883), a pioneering company developing innovative products for the treatment of rare genetic diseases ...

The company seems to be doing everything it's supposed to be doing; the stock just isn't responding.

Add Yahoo as a preferred source to see more of our stories on Google. FILE - This undated photo shows Terry Horgan of Montour Falls, N.Y. Horgan, 27, the lone volunteer in a gene-editing study ...

Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. On August 24 in the journal Stem Cell Reports, researchers show how a dual CRISPR ...